Rare Disease Research:

Most patients with severe and life-threatening rare diseases live with no effective treatment options and no hope.  Clinical trials investigate potential new therapies that may offer hope to people who haven’t yet found a therapy that works or that they can tolerate.

hopeful woman with rare disease
Enter your email if you would like Alexion to contact you about a clinical trial:       

Our Goal.

Alexion Pharmaceuticals, Inc. is committed to research in rare diseases, and investigating 
potential new treatments that have the possibility of transforming patients' lives.

Contact Us

Contact Alexion at clinicaltrials@alexion.com and please specify which study you are interested in.

Click here to find the locations of studies that are actively recruiting


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